Avtor/Urednik     Tesch, Victoria Katharina; Abolhassani, Hassan; Shadur, Bella; Zobel, Joachim; Mareika, Yuliya; Sharapova, Svetlana; Karakoc-Aydiner, Elif; Rivière, Jacques G.; Garcia-Prat, Marina; Moes, Nicolette; Avbelj, Magdalena
Naslov     Long-term outcome of LRBA deficiency in 76 patients after various treatment modalities as evaluated by the immune deficiency and dysregulation activity (IDDA) score
Tip     članek
Vol. in št.     Letnik 145, št. 5
Leto izdaje     2020
Obseg     str. 1452-1463
ISSN     0091-6749 - The Journal of allergy and clinical immunology
Jezik     eng
Proste vsebinske oznake     inborn error of immunity
primary immunodeficiency disorder
immune dysregulation
clinical score
performance scale
hematopoietic stem cell transplantation
CTLA4
abatacept
sirolimus
combined immunodeficiency