Author/Editor     Žerjav-Tanšek, Mojca; Battelino, Tadej; Grošelj, Urh; Kelvišar, Matic; Kobe, Helena; Repič-Lampret, Barbka
Title     Long-term BH4 (sapropterin) treatment of children with hyperphenylalaninemia-effect on median Phe/Tyr ratios
Type     članek
Vol. and No.     Letnik 29, št. 5
Publication year     2016
Volume     str. 561-566
ISSN     0334-018X - Journal of pediatric endocrinology & metabolism : JPEM
Language     eng
Keywords     BH4
hyperphenylalaninemia
phenylketonuria
sapropterin