Author/Editor     Golli, Tanja; Butenko, Tita; Loboda, Tanja; Osredkar, Damjan
Title     One-year follow-up of Slovenian DMD patients treated with Ataluren
Type     članek
Source     In: Abstract book : EPNS 2019 Athens : European Paediatric Neurology Society
Publication year     2019
Volume     str. 303
Language     eng
Keywords     Duchennova mišična distrofija (DMD)
Ataluren
slovenski bolniki z DMD
Duchenne muscular dystrophy (DMD)
Ataluren
Slovenian DMD patients