Author/Editor | Golli, Tanja; Butenko, Tita; Loboda, Tanja; Osredkar, Damjan | |
Title | One-year follow-up of Slovenian DMD patients treated with Ataluren | |
Type | članek | |
Source | In: Abstract book : EPNS 2019 Athens : European Paediatric Neurology Society | |
Publication year | 2019 | |
Volume | str. 303 | |
Language | eng | |
Keywords | Duchennova mišična distrofija (DMD) Ataluren slovenski bolniki z DMD Duchenne muscular dystrophy (DMD) Ataluren Slovenian DMD patients |