Author/Editor		Gentner, Bernhard; Tucci, Francesca; Galimberti, Stefania; Fumagalli, Francesca; De Pellegrin, Maurizio; Silvani, Paolo; Camesasca, Chiara; Pontesilli, Silvia; Darin, Silvia; Ciotti, Francesca; Grošelj, Urh
Title		Hematopoietic stem- and progenitor-cell gene therapy for Hurler syndrome
Type		članek
Vol. and No.		Letnik 385, št. 21
Publication year		2021
Volume		str. 1929-1940
ISSN		0028-4793 - The New England journal of medicine
Language		eng
Keywords		Hurlerjev sindrom zdravljenje z matičnimi celicami mukopolisaharidoze redke bolezni zdravljenje