Author/Editor     Zver, Aleksandra; Lepej, Dušanka; Kotnik Pirš, Ana; Praprotnik, Marina; Šetina Šmid, Saša; Butenko, Tita; Osredkar, Damjan; Krivec, Uroš
Title     Respiratory and nutritional effects of nusinersen treatment in spinal muscular atrophy patients
Type     članek
Vol. and No.     Letnik 56Letnik suppl. 2
Publication year     2021
Volume     str. S131
ISSN     1054-187X - Pediatric pulmonology. Supplement
Language     eng
Keywords     spinal muscular atrophy
Nusinersen
respiratory and nutritional effects
spinalna mišična atrofija
Nusinersen
dihalni in prehranski učinki